STERIALS

The company is a biotechnology company engaged in the development, manufacture and sale of pharmaceutical products to treat the underlying causes of chronic genetic diseases, including cystic fibrosis, sickle cell disease and transfusion-dependent beta thalassemia, as well as the development of treatments for other serious diseases, including APOL1-mediated kidney disease, acute and neuropathic pain, type 1 diabetes, type 1 myotonic dystrophy and alpha-1 antitrypsin deficiency.